Patients & Community
Zogenix is working to develop therapies with the potential to transform the lives of patients and their families living with serious rare diseases.
- Clinical Studies – Zogenix is not currently enrolling patients in studies for Dravet syndrome.
- EAP – We offer a limited expanded access program (also known as “compassionate use” or “early access”) for our investigational therapy ZX008. Requests for access to experimental therapies must be made by a qualified and licensed physician. Learn More
- Disease – For more information about the US Dravet Syndrome Foundation, click here. For more information about the Dravet Syndrome European Federation, click here.
- Additional Resources – For more information about Dravet Syndrome, please see the Dravet Syndrome, and Dravet Syndrome Caregiver factsheets
Lennox-Gastaut Syndrome (LGS)
CDKL5 Deficiency Disorder (CDD)
A rare and severe epilepsy
CDKL5 deficiency disorder is a rare developmental epileptic encephalopathy caused by mutations in the CDKL5 gene which can manifest in a broad range of clinical symptoms and severity. The hallmarks are early-onset, intractable epilepsy and neurodevelopmental delay impacting cognitive, motor, speech, and visual function. Although rare, the occurrence is believed to be ~1:40,000 -60,000 live births, making it one of the most common forms of genetic epilepsy.[i]
- Clinical Studies – Zogenix is currently enrolling patients for a clinical studies CDD. For more information: https://www.CDDstudy.com
- Registries & Natural History Studies – To help advance CDKL5 research and gain better insights on your child or loved one with CDKL5 Deficiency Disorder, please consider signing up to help the researchers: https://www.cdkl5.com/help-our-researchers/.
- Disease – For more information about CDKL5 deficiency disorder, please visit the International Foundation for CDKL5 Research (IFCR) or the LouLou Foundation.
- Clinical Studies – Zogenix is not yet enrolling for Phase 3 trials of MT1621, its investigational treatment for TK2 deficiency.
- Registry – Take on TK2D –Whether you’re living with an MDS, have been diagnosed with TK2d, or are a parent, caregiver, or healthcare professional (HCP) who wants to learn more about MDS and TK2d, join the registry so we can all take on TK2d together.
- Disease – For more information about TK2 deficiency, please visit tk2d.com. Or visit the United Mitochondrial Disease Foundation at https://www.umdf.org/
- Additional Resources – Understanding TK2d